Gene Therapy Whitepaper

Of the many notable medical breakthroughs in the last decade, few have elicited more genuine

hope than the promise of gene therapies for rare diseases.


Access our latest whitepaper, authored by Orsini Founder & CEO, Mike Fieri, and get a personal perspective on how gene therapies are guiding the future of treatment for rare diseases, including:

  • Duchenne Muscular Dystrophy (DMD)

  • Hereditary Angioedema (HAE)

  • Idiopathic Pulmonary Fibrosis (IPF)

  • Spinal Muscular Atrophy (SMA)

  • Gaucher’s Disease Type 1

  • Mucopolysaccharidosis (MPS)

  • Fabry Disease

  • Pompe Disease

Simply submit your information to immediately access your digital copy of the whitepaper.


Access the Whitepaper